Resverlogix Corp. · TSX:RVX

Resverlogix — ERA-EDTA 2020

25 slides from Resverlogix's conference presentation, Jun 9, 2020

  1. Slide 1: Effects of the BET-Inhibitor Apabetalone on Cardiovascular Events in Type 2 Diabetes and ACS

    TO001 - Free Communication Session S 38 Cardiovascular and renal protection - effects of SGLT2 inhibitors and GLP-1 receptor agonists in people with CKD and type 2 diabetes EFFECTS OF THE BET-INHIBITOR APABETALONE ON CARDIOVASCULAR EVENTS IN PATIENTS WITH TYPE 2 DIABETES MELLITUS AND ACUTE CORONARY

  2. Slide 2: BETonMACE Committees

    BETonMACE Committees Clinical Steering Committee Contributions from 13 countries at 195 sites: K. K. Ray S. J. Nicholls H. Ginsberg K. Kalantar- Country National Lead (Chair) Zadeh Investigator(s) P. Toth K. Buhr (Independent Statistician) G. G. Schwartz Argentina A. Lorenzatti, M. Vico Non- Voting

  3. Slide 3: BETonMACE Background & Rationale

    BETonMACE Background & Rationale • Bromodomain and extraterminal proteins are epigenetic regulators of gene transcription. Chromosome Chromatin Fiber Nucleosome Writers • Epigenetics refers to modifications to chromatin that regulate its activity Histone Tail • Transcription is regulated by Erasers

  4. Slide 4: BET Inhibition by Apabetalone

    BET Inhibition by Apabetalone BET Protein Recruits Apabetalone Apabetalone Gene Transcription Gene Binds Additional Inhibits Acetylated Transcription Transcription Treatment BET Protein Complex Transcription Activated Disrupted Inhibited Histone Factors Activity BET P-TEFb Protein Pol II TF Apabetal

  5. Slide 5: BET Protein Inhibition with Apabetalone Favorably Impacts Pathways in Cardiovascular and Kidney Disease

    BET Protein Inhibition with Apabetalone Favorably Impacts Pathways Implicated in Cardiovascular and Kidney Disease Apabetalone reduces the Treatment with apabetalone expression of multiple reduces mediators that drive components of the complement endothelial activation, monocyte cascade Complement V

  6. Slide 6: Phase 2 Trials Suggest Potential CV Benefit with Apabetalone

    Phase 2 Trials Suggest Potential CV Benefit with Apabetalone MACE Incidence in Total Patient Group MACE Incidence by Presence of Diabetes • MACE (major adverse cardiovascular events) including death, myocardial infarction, coronary revascularization, and hospitalization for cardiovascular causes). •

  7. Slide 7: BETonMACE Inclusion and Exclusion Criteria

    BETonMACE Inclusion and Exclusion Criteria Key Inclusion Criteria Key Exclusion Criteria • Type 2 Diabetes Mellitus • Planned further coronary revascularization at time of screening visit – HbA1c >6.5% or history of diabetes medication use • Previous or current diagnosis of severe heart failure (New

  8. Slide 8: Study Endpoints

    BETonMACE Study Endpoints • Primary Endpoint – Time to first occurrence of CV death or non-fatal MI or stroke • Pre-specified sensitivity analysis excluding deaths of undetermined cause from endpoint • Key Secondary Endpoints – Time to first 4-part MACE: primary endpoint + hospitalization for CV eve

  9. Slide 9: Statistical Assumptions

    Statistical Assumptions • A sample size of 2,400 randomized subjects was predicted to yield 80% power for the primary analysis under the following assumptions: – Total number of events: 250 – 2-sided type 1 error rate: α=5% – 10.5% event rate in the placebo arm at 18 months – 30% relative risk reduc

  10. Slide 10: Study Design

    BETonMACE Study Design Screening Follow-Up Period Treatment Period Period Placebo n = 1,206 Active Arm: apabetalone 100 mg b.i.d + standard of care 1:1 Randomization End of Treatment N=2425 Statin Run-in 40-80 mg Placebo Arm: atorvastatin or matching placebo 20-40 mg + rosuvastatin standard of care

  11. Slide 11: Baseline Characteristics

    BETonMACE Baseline Characteristics Apabetalone Placebo (n=1212) (n=1206) Median age, yrs 62.0 62.0 Male sex- % 74.8 74.0 Body mass index, kg/m2 30.2 30.3 Hypertension - % 89.4 87.8 eGFR Mean ± SD, mL/min/1.73m2 104.9 101.7 Duration of diabetes – yrs 8.4 8.7 Index acute coronary syndrome – % Myocardi

  12. Slide 12: Primary Efficacy Endpoint

    BETonMACE Primary Efficacy Endpoint • CV Death, Non-Fatal MI and Stroke (Total number of events = 274) Median follow-up of 26.5 months Primary Endpoint: Placebo = 12.4% Apabetalone = 10.3% Ray KK, Nicholls SJ, Buhr KA, Ginsberg HN, Johansson JO, Kalantar-Zadeh K, Kulikowski E, Toth PP, Wong N, Sween

  13. Slide 13: Prespecified Primary End Point Sensitivity Analysis Excluding Deaths of Undetermined Cause

    Prespecified Primary End Point Sensitivity Analysis Excluding Deaths of Undetermined Cause CV Death (excluding death of undetermined cause), non-fatal MI, or stroke Ray KK, Nicholls SJ, Buhr KA, Ginsberg HN, Johansson JO, Kalantar-Zadeh K, Kulikowski E, Toth PP, Wong N, Sweeney M, Schwartz GG, Inves

  14. Slide 14: Primary Endpoint in Prespecified Subgroups

    Primary Endpoint in Prespecified Subgroups Subgroup Apabetalone Placebo Hazard Ratio (95% CI) P Value no. of events/patients (%) Sex Female 23/305 (7.5%) 32/313 (10.2%) 0.79 [0.46, 1.36] 0.70 Male 102/907 (11.2%) 117/893 (13.1%) 0.84 [0.64, 1.10] Statin Rosuvastatin 62/591 (10.5%) 71/586 (12.1%) 0.8

  15. Slide 15: BETonMACE Summary

    BETonMACE Summary • Apabetalone did not have a significant effect on incidence of the primary endpoint (CV death, non-fatal MI or stroke) – Lower than anticipated event rate in placebo group (9.7% observed, 10.5% predicted at 18 months) – Study was powered on a 30% reduction in risk of primary endpo

  16. Slide 16: Baseline Demographic Data of the CKD Subgroup

    Baseline Demographic Data of the CKD Subgroup eGFR ≥ 60 eGFR < 60 P-value Placebo Apabetalone (CKD Stage 3-4) (eGFR <60) (eGFR <60) N N=2,125 N=288 N=164 N=124 Age (yr) 61 (54-67) 71 (65-76) <0.001 70.6 (7.9) 69.8 (7.9) Sex Male 1,628 (76.6) 168 (58.3) <0.001 91 (56%) 76 (63%) Race White 1,879 (88.4

  17. Slide 17: CKD Group - Results

    BETonMACE CKD Group - Results • CKD vs. non-CKD patients were older (71 vs. 61 years, P<0.001) with more females (42% vs. 23%, P<0.001) and self-identified non-white patients (18% vs. 12%, P<0.001). • CKD patients had a longer mean duration of diabetes (11.3 vs. 8.2 years, P<0.001) and were less lik

  18. Slide 18: Hazard Ratios for Composite and Component Events by CKD Group

    Hazard Ratios (HR) for Composite and Component Events by CKD Group eGFR < 60 eGFR ≥ 60 Placebo Apabetalone HR Placebo Apabetalone HR Evt/n (%) Evt/n (%) (95% CI) Evt/n (%) Evt/n (%) (95% CI) MACE 35/164 (21.3) 13/124 (10.5) 0.50 [0.26,0.96] 114/1041 (11.0) 112/1084 (10.3) 0.94 [0.73,1.22] MACE + HCH

  19. Slide 19: BET on MACE CKD group - Results

    BET on MACE CKD group - Results • Under placebo, CKD patients exhibited higher CVD prevalence, i.e. – 35/164 (21.3%) vs.114/1041 (11.0%) (HR=2.40, 95% CI [1.67, 3.44]) for ischemic CVD/MACE – 14/164 (8.5%) vs. 34/1041 (3.3%) (HR=3.19, 95% CI [1.66,6.12], P<0.001) for HCHF. • Under apabetalone, CKD g

  20. Slide 20: Kaplan-Meier Estimates by CKD/Non-CKD for MACE

    Kaplan-Meier Estimates by CKD/Non-CKD for MACE Apabetalone Compared to Placebo MACE: Composite of CV death, non-fatal MI and stroke CKD Group (eGFR < 60) Apabetalone CKD Group (eGFR<60) Placebo Placebo Events - 35/164 (21.3%) Apabetalone Events - 13/124 (10.5%) Hazard Ratio = 0.50 [95%CIs: 0.26,0.96

  21. Slide 21: Kaplan-Meier Estimates: Hospitalizations for Congestive Heart Failure

    Kaplan-Meier Estimates by CKD/Non-CKD for MACE Apabetalone Compared to Placebo Hospitalizations for Congestive Heart Failure (HCHF) CKD Group (eGFR < 60) Apabetalone CKD Group (eGFR<60) Placebo Non-CKD Group (eGFR ≥ 60) Placebo Events - 14/164 (8.5%) Apabetalone Placebo Apabetalone Events - 3/124 (2

  22. Slide 22: Kaplan-Meier Estimates: Composite MACE and HCHF

    Kaplan-Meier Estimates by CKD/Non-CKD for MACE Apabetalone Compared to Placebo Composite of CV death, non-fatal MI, stroke and hospitalizations for Congestive Heart Failure (HCHF) CKD Group (eGFR < 60) Apabetalone Placebo CKD Group (eGFR<60) Placebo Events - 41/164 (25.0%) Apabetalone Events - 3/124

  23. Slide 23: Safety of Apabetalone in CKD Patients

    Safety of Apabetalone in CKD Patients • Apabetalone was well tolerated with similar number a subjects in both groups experiencing AE’s [119 (72.6%) and 88 (71.0%) in the placebo and apabetalone groups, respectively]. • A significantly lower number of subjects in the apabetalone group had serious adv

  24. Slide 24: Limitations of the CKD Study

    Limitations of the CKD Study • Relatively small portion of the parent trial: 288 CKD patients out of 2,425 • Less balanced randomization among 288 CKD patients • Limited to CKD Stages 3a and 3b (given exclusion criteria of eGFR<30 ml/min/1.73) • Lack of urine data: No albuminuria data were collected

  25. Slide 25: Conclusions

    Conclusions • This is the first cardiovascular outcomes trial assessing the potential of epigenetic modification with BET protein inhibition “apabetalone” and shows promise • In this Phase III RCT, diabetic CKD patients with a recent acute coronary syndrome (ACS) exhibited a high prevalence of CVD (

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